The AHC Research Program

Our Strategy

A hub to centralize, grow, and accelerate research. A portfolio approach to maximize the probability of success. A patients-as-partners model to center research on patient priorities.

Alternating Hemiplegia of Childhood

A representative disorder with a spectrum of neurological symptoms.

Research

A strategically assembled portfolio spanning mechanistic science, resource- and tool-building, and a range of preclinical therapeutics testing in cell and animal models of AHC.

Patient Data

A growing registry of 200+ patients. Patient-reported data on symptom prevalence, paroxysmal symptom frequency, duration, and burden. Analysis of patient priorities.